Category Archives: DMTsDetail

Glatiramer acetate

Summary

Glatiramer acetate (GA) has been an injectable workhorse of MS treatment for decades, alongside the interferon-beta preparations. It is moderately effective; only a minority of people with MS receiving GA achieve long-term NEIDA (no evident inflammatory disease activity). Its impact on preventing end-organ damage (brain volume loss) is modest.

In general, GA formulations are relatively well tolerated in the short-term, the main issues being injection site reactions, occasional flushing reactions with tightness of the chest, swelling of lymph nodes and (rarely) urticaria or hives. However, long-term use of GA leads to lipoatrophy (loss of fatty tissue under the skin). Major advantages are that GA has no monitoring requirements, and it is safe during pregnancy. Adherence has been a problem in the long term, owing to injection fatigue. Given that more effective DMTs are now available, with more favourable attributes, most people with MS now tend to choose non-injectable treatments. Despite this, there is still a role for GA in treating MS, particularly in women who are planning to start or extend their family.

Trade names

Copaxone, Brabio.

Mode of action

Immunomodulatory. GA is often referred to as the DMT with nine or more modes of action, because so many different effects on the immune system have been linked to it. Importantly, none of these immunological changes is associated with immunosuppression.

Efficacy

Moderate.

Class

Maintenance, immunomodulatory.

Immunosuppression

No.

Dosing

  • GA-20 mg, prefilled syringe, 20 mg/mL subcutaneous (SC) daily.
  • GA-40 mg, prefilled syringe, 40 mg/mL SC three times per week.

Main adverse events

Injection site reactions are the most frequent adverse events, with redness, pain, itching, swelling and (rarely) breakdown of the skin. Following prolonged injecting, lipoatrophy and skin necrosis may occur. Occasionally patients may experience an immediate reaction post injection, with flushing, chest tightness, shortness of breath, palpitations and a rapid heart rate.

Adverse events of special interest

  • Swelling of lymph nodes (pseudolymphoma).
  • Urticaria or hives.

Neutralizing antibodies (NAbs)

No.

Pharmacovigilance monitoring requirements 

  • Baseline: none.
  • Follow-up: none.

Rebaselining

A rebaseline MRI needs to be done after GA has had sufficient time to work, ideally ~7 ̶ 12 months after starting treatment. GA is the one maintenance DMT that takes quite a long time to reach maximum effectiveness evident on MRI. I recommend including Gd-enhancement as part of the MRI. The presence of Gd-enhancing lesions on the rebaseline scan is sufficient evidence at this stage to switch/escalate treatment to another DMT.

Pregnancy

No known reproductive toxicity. Generally considered to be safe in pregnancy. In case of unplanned pregnancy while receiving GA, termination of the pregnancy is unnecessary. Most neurologists recommend continuing GA treatment throughout pregnancy.

Breastfeeding

Safe, not contraindicated.

Male fertility

Safe.

Vaccination

Safe.

Summaries of Product Characteristics (SmPC)

Copaxone 20 mg, Copaxone 40 mg, Brabio 20 mg, Brabio 40 mg

Switching-2-GA

GA-20 to GA-40 switch

People with MS may decide to switch between GA preparations because of local skin reactions. GA-40 is administered only three times per week and has demonstrated better tolerability than the daily GA-20 formulation.

Lack of efficacy

I would not recommend switching between GA preparations because of lack of efficacy or perceived lack of efficacy. If you have had a suboptimal response to one GA preparation it would make sense to switch classes. In general, I tend to escalate treatment rather than switch to another moderate efficacy DMT; vertical escalation rather than horizontal switching

Other DMTs

Provided the baseline screening blood tests are fine and there are no specific contraindications, I see no reason why GA can’t be used after any of the other licensed DMTs. However, if you are switching due to a suboptimal response, I would recommend a more efficacious DMT. There is reasonable real-life data that shows switching upwards (escalation) gives a better overall response rate than switching to a similar efficacy DMT (horizontal switching). I suspect that most people with MS who switch to GA will do so for family planning reasons, because GA has one of the best safety records in pregnancy. Another reason to switch may be an adverse event on another DMT, for example persistent lymphopaenia.

Special circumstances

The presence of other specific comorbidities may make it difficult to switch from certain DMTs to GA. These could include generalised urticaria or a known allergic reaction to GA in the past.

Interferon-beta

Summary

Interferon-beta (IFN-beta) preparations have been the workhorse of MS treatment for decades. They are moderately effective; only a minority of people with MS receiving IFN-beta achieve long-term NEIDA (no evident inflammatory disease activity). Their impact on preventing end-organ damage (brain volume loss) and reducing neurofilament levels (an indicator of damaged nerve fibres) is modest. In general, IFN-beta formulations are poorly tolerated in the short-term owing to injection site reactions and flu-like side effects, but both these side effects can be effectively managed in most people with MS. Monitoring requirements are not too onerous. Adherence has been a problem long-term owing to injection fatigue. IFN-beta is a biological so it can induce neutralising antibodies (NAbs), the rate of which varies according to the different formulations.

IFN-beta belongs to the class of cytokines and is produced by the body to help fight infections, particularly viral infections and possibly cancers. IFN-beta also plays a role in foetal bone development. I have long had concerns about the potential of anti-IFN-beta NAbs to neutralise one’s own IFN-beta and to cross the placenta and affect the role of IFN-beta in foetal development. Therefore, I have favoured the formulations with the lowest NAb rates. Given that more effective DMTs are now available, with more favourable attributes, most people with MS tend to choose other, non-injectable treatments. Despite this, there is still a role for IFN-beta preparations in the treatment of MS, particularly as they have now been shown to be safe in pregnancy.

Trade names

Avonex (IFN-beta-1a), Betaferon (IFN-beta-1b), Betaseron (IFN-beta-1b), Extavia (IFN-beta-1b), Plegridy (Peg-IFN-beta-1a), Rebif (IFN-beta-1a).

Mode of action

Immunomodulatory, with many different effects on the immune system. In general, IFN-beta is not immunosuppressive.

Efficacy

Moderate.

Class

Maintenance, immunomodulatory.

Immunosuppression

No.

Dosing 

  • IFN-beta-1b (Betaseron, Betaferon, Extavia; continuous type 1 interferon receptor stimulation and downregulation), freeze-dried, 250 micrograms (µg) subcutaneous (SC) alternate days.
  • IFN-beta-1a (Avonex; pulsatile, type 1 interferon stimulation), prefilled syringe, 30 µg IM weekly.
  • IFN-beta-1a (Rebif; continuous type 1 interferon receptor stimulation and downregulation), prefilled syringe or cartridge, 22/44 µg SC three times a week.
  • Peg-IFN-beta-1a (Plegridy; pegylated hence long-circulating half-life with continuous type 1 interferon receptor stimulation), prefilled syringe 125 µg SC or IM every 2 weeks.

Main adverse events

Injection site reactions, flu-like symptoms, abnormal liver function tests (LFTs), low lymphocyte counts (lymphopaenia), and low white cell counts (leukopaenia).

Rare adverse events of special interest

  • Thrombotic microangiopathy, which manifests as so-called thrombotic thrombocytopenic purpura or haemolytic ̶ uraemic syndrome (i.e. low platelet levels, blood clots, bruising and renal failure).
  • Liver failure or autoimmune hepatitis.
  • Pulmonary oedema, or capillary leak syndrome, in patients with a monoclonal gammopathy.
  • Severe bone marrow suppression.

Neutralising antibodies (NAbs)

Yes; ~30% IFN-beta-1b (Betaseron, Betaferon, Extavia), 12 ̶ 25% IFN-beta-1a (Rebif), <5% IFN-beta-1a (Avonex), and <2% Peg-IFN-beta-1a (Plegridy).

Pharmacovigilance monitoring requirements

Baseline

  • Full blood count, urea and electrolytes, liver function tests, thyroid function tests, serum protein electrophoresis, renal protein.

Follow-up

  • 1-month, 3-months, 6-months and then 6-monthly while on the treatment: FBC, U&E and LFTs
  • 12-monthly: TFTs
  • 12- and 24-monthly: NAbs.

Rebaselining

A rebaseline MRI needs to be done after IFN-beta has had sufficient time to work, ideally 6 months after starting treatment. I recommend including Gd-enhancement as part of the MRI. The presence of Gd-enhancing lesions on the rebaseline scan is sufficient evidence at this stage to switch/escalate treatment to another DMT, that is, it tells you that the treatment is failing to suppress inflammatory disease activity.

Pregnancy

There is a small increased risk of spontaneous abortion in women who are on IFN-beta when they fall pregnant. Initiation of treatment is not recommended during pregnancy. In case of unplanned pregnancy while receiving IFN-beta, termination of the pregnancy is not necessary, and many neurologists recommend continuing IFN-beta treatment throughout pregnancy.

Breastfeeding

Safe, not contraindicated.

Male fertility

Safe.

Vaccination

Safe.

Summaries of Product Characteristics (SmPC)

Betaferon (Europe), Betaseron (USA), Extavia (IFN-beta-1b); Avonex, Rebif, Plegridy (IFN-beta-1a); interferon-beta.

Switching-2-IFN-beta

IFN-beta to IFN-beta switch

The only reason to switch between IFN-beta preparations is for local, or systemic, intolerance. Many patients with local skin, or injection site, reactions move to intramuscular IFN-beta-1a (Avonex), which does not cause local skin reactions. In contrast, many patients move from IFN-beta-1a (Avonex) to IFN-beta-1a (Rebif) or -1b (Betaferon) because of persistent flu-like reactions. Because Avonex allows the interferon receptors to regenerate before the next injections, mild flu-like symptoms can persist; this does not happen with Rebif and Betaferon. Betaferon is administered on alternate days; however, Rebif is given three times per week, and some patients experience mild flu-like side effects after the 2-day injection break (once each week) but not after a 1-day break (twice each week).

NAbs

If you have developed NAbs to one IFN-beta preparation these cross-react with the other preparations. In this situation NAbs would simply neutralise the effect of a new IFN-beta formulation.

Lack of efficacy

I would not recommend switching between IFN-beta preparations because of lack of efficacy or perceived lack of efficacy. If you have had a suboptimal response to one IFN-beta preparation, it will make sense to switch classes. I generally tend to escalate treatment to a more efficacious DMT rather than switch to another moderate efficacy DMT: vertical escalation rather than horizontal switching.

Other DMTs

Provided the baseline screening blood tests are fine and there are no specific contraindications, I see no reason why IFN-beta can’t be used after any of the other licensed DMTs. Apart from NAbs inhibiting the action of other IFN-beta formulations, I am not aware that a failure to respond to a different DMT predicts a lack of response to another IFN-beta. However, if you are switching due to a suboptimal response, I would recommend a potentially more efficacious DMT. There is reasonable real-life data that shows switching upwards (escalation) gives a better overall response rate than switching to a similar efficacy DMT (horizontal switching).

Special circumstances

The presence of some specific comorbidities or adverse events may make it difficult to switch from one DMT to IFN-beta. For example, a persistent low lymphocyte count (<800), low neutrophil count (<1,000), low total white cell count (<1,500) and/or abnormal LFTs, that can occur with several DMTs, are relative contraindications to IFN-beta. Similarly, the presence of a monoclonal gammopathy (abnormal protein in the blood) is a contraindication to IFN-beta due to the risk of capillary leak syndrome (fluid on the lungs).